Correction of multi-gene deficiency in vivo using a single 'self-cleaving' 2A peptide–based retroviral vector
Published Online: 2004-04-04
Journal: Nature Biotechnology•Publisher: Springer Science and Business Media LLC
Authors: Andrea L Szymczak•Creg J Workman•Dario A A Vignali•Elio F Vanin•Kate M Vignali•Smaroula Dilioglou•Yao Wang